You may qualify for the EMPOWERS clinical research study if you:
  • Are at least 18 years old
  • Have attenuated MPS I
  • Are able and willing to use corticosteroids

People who qualify will receive:

  • Investigational gene therapy (SB-318) for MPS I
  • Study-related medical care
  • Reimbursement for travel (Transportation assistance may be available)


To learn more about the study opportunity, please contact Contact Us
Find a Study Doctor

United States, California
UCSF Benioff Children’s Hospital Oakland
Oakland, California, United States, 94609
Contact: Jill Nicholas
510-428-3885 ext 5241
Principal Investigator: Paul Harmatz, MD

United States, Florida
University of Florida
Gainesville, Florida United States, 32610
Contact: Gee Kim
Principal Investigator: Coy Heldermon, MD

United States, Georgia
Emory University
Decatur, Georgia 30033
Contact: Stephanie Cagle
Principal Investigator: William Wilcox, MD

United States, Minnesota
University of Minnesota
Minneapolis, Minnesota, United States, 55455
Contact: Patricia Grover
612-672-5151 ext 5241
Principal Investigator: Chester B Whitley, PhD, MD

United States, New York
NYU School of Medicine
New York, New York, United States, 10016
Contact: Sara Rodriguez
Principal Investigator: Heather A Lau, MD

United States, Ohio
Cincinnati Children’s Hospital Medical Center
Cincinnati, Ohio, United States, 45229
Contact: Laurie Bailey
Principal Investigator: Nancy Leslie, MD

Think the EMPOWERS study may be for you?

Find a Study Doctor